Re: Recent Nature blog on Sangamo and Huntington's disease
Phillip Gregory => “The next step is to make that sure they operate at a broad range of doses, and then we need to move into animal studies of efficacy and safety.”
Gruenwald => "One challenge is that targeting viral vectors to specified brain areas and then ensuring their proper distribution is difficult, and this is further complicated by the fact that Huntington’s disease begins in deep brain structures before spreading to the cerebral cortex."
Anybody here betting we will see an IND for Huntington's in the next two years?
-bin