Avanir/Concert | AVP-786 | Dextromethorphan | NMDA glutamate receptor | Alzheimer's disease agitation symptoms | Phase 3 |
Depression/schizophrenia | Phase 2 |
Concert | CTP-543 | Ruxolitinib | JAK/STAT | Hair loss (alopecia aerate) | Phase 2 |
Vertex | CTP-656 | Kalydeco (ivacaftor) | CF transmembrane conductor regulator | Cystic fibrosis | Phase 2 |
DeuteRx | DRX-065 | Pioglitazone (deuterated form) | (PPAR-γ) | Non-alcoholic steatohepatitis/adrenoleukodystrophy | Phase 1 |
Retrotope | RT001 | Linoleic acid | Cell membrane | Freidreich's ataxia | Phase 1/2 |
BMS | BMS-986165 | Rosuvastatin | Tyrosine kinases | Psoriasis | Phase 2 |
Celgene/Concert | CT-730 | Apremilast | PDE4 | Inflammatory disorders | Phase 1 |
Vertex | VX-984 | Doxorubicin | DNA-dependent protein kinase | Solid tumors | |