Re: Bonus: We've got the Holy Grail.
Well, we've yet to see definitive proof gene therapy works and is safe. Hopefully this stuff they've determined is both. The PPMO news is most exciting to me because it brings back the good old days around here: finally, we can start to dream big again! And you could hear that in Ed's voice at the end of both presentations when he got into it. ".... and not just muscles ...." Not that there's anything wrong with muscles but muscles is only where this starts ....