Re: Competition...sickle cell disease
SGMO doesn't even have an IND for sickle cell. Meanwhile other companies are developing small molecules to treat this disease. a lot can be made globally well before SGMO even gets a registrational trial underway.
"Sangamo intends to file a new Investigational New Drug (IND) application for the "BCL11A Enhancer" approach for beta-thalassemia and anticipates initiating a Phase 1 clinical trial in 2016."
Today, being the leader is much shorter than ever if you have no plan to stay ahead. The competition is quickly catching up and passing SGMO.
https://clinicaltrials.gov/ct2/show/NCT02186418?term=sickle+cell&rank=6
https://clinicaltrials.gov/ct2/show/NCT02380079?term=sickle+cell&type=Intr&fund=2&rank=29